--- title: "Passage Bio reports biomarker improvements, FDA says randomized registrational trial required" type: "News" locale: "en" url: "https://longbridge.com/en/news/283343631.md" description: "Passage Bio reported interim data from its upliFT-D study, showing significant reductions in brain atrophy and stabilization of plasma NfL levels with PBFT02. CDR-1 patients experienced a 64% reduction in whole brain atrophy and a 54% reduction in frontotemporal atrophy at 12 months. The FDA indicated that a randomized controlled registrational study is necessary, prompting the company to evaluate next steps and engage in a strategic review with Wedbush PacGrow." datetime: "2026-04-20T11:23:00.000Z" locales: - [zh-CN](https://longbridge.com/zh-CN/news/283343631.md) - [en](https://longbridge.com/en/news/283343631.md) - [zh-HK](https://longbridge.com/zh-HK/news/283343631.md) --- # Passage Bio reports biomarker improvements, FDA says randomized registrational trial required **Passage Bio reported updated upliFT-D interim data showing reduced brain atrophy and stabilized plasma NfL with PBFT02.** **Key Highlights:** - PBFT02 CDR‑1 patients showed 3.1% whole brain atrophy at 12m vs 8.7% in ALLFTD NH (64% reduction; n=2 vs n=7). - PBFT02 CDR‑1 patients showed 4.6% frontotemporal atrophy at 12m vs 9.9% in ALLFTD NH (54% reduction; n=2 vs n=7). - Plasma NfL stabilized in treated patients: mean −1.0 pg/mL at 12m (n=6) vs +13.5 pg/mL in ALLFTD natural history (n=7). - Dose 1 (4.5e13 GC) produced durable CSF progranulin increases to mean 22.8 ng/mL at 12m (n=6) and 24.2 ng/mL at 18m (n=3); Dose 2 showed comparable levels by 6m. - FDA Type C meeting: agency indicated a randomized controlled registrational study will be required; company is evaluating next steps and initiated a strategic review with Wedbush PacGrow engaged. Original SEC Filing: Passage BIO, Inc. \[ PASG \] - 8-K - Apr. 20, 2026 **Disclaimer** This is an AI-powered summary. It may contain inaccuracies. Consider verifying important information with the source. Please note this summary is solely based on documents filed with the SEC. ### Related Stocks - [PASG.US](https://longbridge.com/en/quote/PASG.US.md) - [BIB.US](https://longbridge.com/en/quote/BIB.US.md) - [LABU.US](https://longbridge.com/en/quote/LABU.US.md) - [IBBQ.US](https://longbridge.com/en/quote/IBBQ.US.md) - [PBE.US](https://longbridge.com/en/quote/PBE.US.md) - [FBT.US](https://longbridge.com/en/quote/FBT.US.md) - [SBIO.US](https://longbridge.com/en/quote/SBIO.US.md) - [IBB.US](https://longbridge.com/en/quote/IBB.US.md) - [BBH.US](https://longbridge.com/en/quote/BBH.US.md) - [XBI.US](https://longbridge.com/en/quote/XBI.US.md) ## Related News & Research - [Rani Therapeutics Q1 contract revenue rises on Chugai collaboration; announces CFO transition](https://longbridge.com/en/news/286608288.md) - [Bicara Therapeutics: 1500mg Ficerafusp Alfa + Pembrolizumab Shows Estimated 31% 3‑Year OS in 1L R/M HPV‑Negative HNSCC](https://longbridge.com/en/news/287274216.md) - [Liminatus Pharma Announces Proposed Merger with InnocsAI to Expand Oncology Cell Therapy Pipeline | LIMN Stock News](https://longbridge.com/en/news/287218720.md) - [BUZZ-Street View: Regeneron's melanoma trial setback raises bigger-picture questions](https://longbridge.com/en/news/286769076.md) - [Roivant posts unexpected Q4 profit due to Moderna lawsuit settlement gain](https://longbridge.com/en/news/287053604.md)