argenx SE Announces Advancement of ARGX-119 to Registrational Study for Congenital Myasthenic Syndromes Following Promising Phase 1b Results

Reuters
2025.06.30 05:00
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argenx SE has announced the advancement of ARGX-119 to a registrational study for congenital myasthenic syndromes (CMS) after positive Phase 1b results. The study showed a favorable safety profile and met its primary endpoint, with improvements noted in secondary endpoints such as the Six-Minute Walk Test and Myasthenia Gravis scores in treated DOK7-CMS patients. Detailed results will be presented at an upcoming medical meeting.