Entrada Therapeutics Unveils Pipeline Progress and Clinical Milestones for Duchenne and Myotonic Dystrophy Programs

Reuters
2025.12.15 17:45
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Entrada Therapeutics Inc. has announced updates on its clinical development pipeline, aiming to advance four clinical-stage programs by the end of 2025. Key milestones in 2026 include data readouts for ENTR-601-44, ENTR-601-45, and progress on ENTR-601-50 and VX-670 for myotonic dystrophy type 1. The company focuses on its EEV platform and novel PMO conjugates, with ongoing and planned ex-U.S. studies to support regulatory discussions and potential accelerated approvals.